Danielle has lived her entire life with sickle cell disease. “My blood cells are like sickle shape instead of like normal ...
Caden Major was born with sickle cell disease – an inherited blood disorder affecting red blood cells. Now at 19 years old, ...
For individuals living with sickle cell disease (SCD), the transition from pediatric to adult care can be one of the most ...
Less than a third of ED visits for acute sickle cell disease pain were guideline-adherent for the timely administration of ...
Major is one of the first pediatric patients in Florida to receive gene therapy for sickle cell disease since the FDA ...
“To provide menstruating patients with sickle cell disease the best care, primary care physicians, gynecologists, and ...
Most people with sickle cell disease who undergo allogeneic hematopoietic cell transplantation achieve favorable long-term ...
Preliminary results from two trials of the gene therapy exagamglogene autotemcel (exa-cel) suggest the therapy offers an ...
Key Highlights Motixafortide effectively mobilized sufficient hematopoietic stem cells (HSCs) in patients with sickle cell disease enabling accelerated access to gene therapies 90% (9 of 10) of ...
Motixafortide alone and in combination with natalizumab (VLA-4 inhibitor) led to robust hematopoietic stem cell (HSC) ...
At ASH 2025, Fulcrum presented promising data on a sickle cell pill and Incyte is pioneering a new way to treat myelofibrosis ...
Multiple copies of a book titled Voices of Sickle Cell, written by Dr Edda Hadeed, President of the Sickle Cell Association ...